Joyce Esser thought she had found her voice again—until an AI speech system took it away for swearing. The UK woman who has bulbar motor neuron disease (MND), used the AI-powered voice cloning tool by ...

A toddler was successfully treated for a rare genetic disease, spinal muscular atrophy, after world-first in-womb therapy.

The Phase 3 EPIC trial is a randomized, sham-controlled, double-blind study evaluating NRTX-1001 cell therapy in adults with ...

Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude ...

Discover the first in-utero treatment for spinal muscular atrophy (SMA) using risdiplam. Promising results show no SMA signs ...

Both my father and his mother were afflicted with Alzheimer’s disease in the later parts of their lives. I watched my father go from a bold ex-Marine who loved to ...

Connor Whitelaw, 23, will take on the hefty trek in memory of his aunt Gwen, a "vibrant lady, loved dearly by family and ...