The study conducted by IIT Roorkee is supported by the Indian Council of Medical Research (ICMR). It has been published in a ...

Converting one type of cell to another—for example, a skin cell to a neuron—can be done through a process that requires the ...

Danon disease is a rare but serious cardiomyopathy that drastically reduces life expectancy. Male patients infrequently live ...

A recent study on T cell gene therapy trials shows that while secondary malignancies occur in a small percentage of patients, ...

A modified herpes virus that targets spinal cord nerve cells to treat neurogenic bladder in people with spinal cord injury is underway in a first-in-human clinical trial by UTHealth Houston at TIRR ...

X-linked severe combined immunodeficiency disease (X-SCID) is a rare genetic disorder characterized by profound defects in ...

“When scaling up a process based on adherent cells, a biopharmaceutical manufacturer has two options. Either stay in 2D, resulting in the use of heavy and difficult-to-handle multi-tray stacks with a ...

In a preclinical study, researchers at Children's Hospital of Philadelphia (CHOP) demonstrated a novel gene therapy with ...

The FDA has accepted for Priority Review the BLA for PRGN-2012 for the treatment of adults with recurrent respiratory papillomatosis.

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

Development strategies designed to reduce the unknowns so that cell and gene therapy innovators can develop robust processes ...

D-150 is a potential backbone therapy that is designed to provide multi-year sustained delivery of anti-VEGF (aflibercept and ...